One of the primary themes of this year's conference is community clinical trial readiness. Small patient populations require community and stakeholder buy-in, and all patients and their families play a vital role in the success of clinical trials. KSF is committed to providing a robust and enriching program and think you’ll find the information delivered by our experts, advocates, and industry experts to be empowering. Here are some of the headlines you can view after registration:
- Understanding the Epigenetics of Kabuki Syndrome and How the disease mechanism of Kabuki syndrome being addressed in the current research landscape. Featuring a series of flash talks and deeper dive discussions on research initiatives that address symptoms of Kabuki syndrome
- Understanding why patient-centered research is important for clinical trial design - with a Special Guest from the National Institute of Health (NIH)
- Neurologic focused clinical trials in the pipeline: An update on the HOPE clinical trial featuring ORYZON and Primary Investigator Dr. Jacqueline Harris
- Neurocognitive and Behavioral tools, resources, and supports that families can explore NOW
- Patients as Partners: Shared learnings from diagnosed individuals who have participated in clinical trials
- Overcoming Adversity: Inspirational fireside chat with adults who are diagnosed with Kabuki syndrome ...and much more!
We are excited to share that an amazing team of renowned researchers, biotechs, patients, and advocates joined the program this year. Live Q&As followed every presentation and are available to watch as well.
Thank you for joining us in our mission to accelerate research toward treatments for Kabuki syndrome.
To view the complete Agenda, CLICK HERE